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Chemical Structure| 72599-27-0 Chemical Structure| 72599-27-0

Structure of Miglustat
CAS No.: 72599-27-0

Chemical Structure| 72599-27-0

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Miglustat is an inhibitor of glucosylceramide synthase, primarily to treat Type I Gaucher disease (GD1).

Synonyms: NB-DNJ; N-Butyldeoxynojirimycin; N‐butyldeoxynojirimycin

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Product Details of Miglustat

CAS No. :72599-27-0
Formula : C10H21NO4
M.W : 219.28
SMILES Code : O[C@H]1[C@H](O)[C@@H](CO)N(CCCC)C[C@@H]1O
Synonyms :
NB-DNJ; N-Butyldeoxynojirimycin; N‐butyldeoxynojirimycin
MDL No. :MFCD00272581
InChI Key :UQRORFVVSGFNRO-UTINFBMNSA-N
Pubchem ID :51634

Safety of Miglustat

GHS Pictogram:
Signal Word:Warning
Hazard Statements:H361
Precautionary Statements:P501-P202-P201-P280-P308+P313-P405

Isoform Comparison

Biological Activity

Clinical Trial:

NCT Number Conditions Phases Recruitment Completion Date Locations
NCT02612129 Niemann-Pick Disease, Type C Phase 2 Phase 3 Active, not recruiting October 2020 United States, California ... More >> UCSF Benioff Children's Hospital Oakland Oakland, California, United States, 94609 United States, Minnesota Mayo Clinic Children's Center Rochester, Minnesota, United States, 55905 Denmark University Hospital Copenhagen (Rigshospitalet) Copenhagen, Denmark, 2100 France CHU de Montpellier Montpellier, France, 34295 Montpellier Cedex 5 Hôpital Trousseau Paris, France, 75571 PARIS Cedex 12 Germany Villa Metabolica Mainz Mainz, Germany, 55131 Dr. von Haunersches Kinderspital der Universität München Munich, Germany, 80337 Italy Ospedale Pediatrico Bambino Gesù Rome, Italy, 00165 Azienda Ospedaliero-Universitaria "Santa Maria della Misericordia" di Udin Udine, Italy, 33100 Poland The Children´s Memorial Istitute Warsaw Warsaw, Poland, 04-730 Spain Hospital Vall D'Hebron Barcelona, Spain, 08035 Switzerland INSELSPITAL University Hospital Bern Bern, Switzerland, CH-3010 United Kingdom Birmingham Children's Hospital Birmingham, United Kingdom, B4 6NH Great Ormond Street Hospital London, United Kingdom, WC1N 3JH Less <<
NCT00000791 HIV Infections Phase 2 Completed - United States, Alabama ... More >> Alabama Therapeutics CRS Birmingham, Alabama, United States United States, California USC CRS Los Angeles, California, United States, 90033 Stanford CRS Palo Alto, California, United States Ucsf Aids Crs San Francisco, California, United States, 94110 United States, Colorado University of Colorado Hospital CRS Aurora, Colorado, United States United States, Florida Univ. of Miami AIDS CRS Miami, Florida, United States United States, Illinois Northwestern University CRS Chicago, Illinois, United States, 60611 Rush Univ. Med. Ctr. ACTG CRS Chicago, Illinois, United States, 60612 Weiss Memorial Hosp. Chicago, Illinois, United States, 60640 Cook County Hosp. CORE Ctr. Chicago, Illinois, United States United States, Indiana Indiana Univ. School of Medicine, Infectious Disease Research Clinic Indianapolis, Indiana, United States Methodist Hosp. of Indiana Indianapolis, Indiana, United States United States, Missouri St. Louis ConnectCare, Infectious Diseases Clinic St. Louis, Missouri, United States, 63112 Washington U CRS St. Louis, Missouri, United States United States, New York SUNY - Buffalo, Erie County Medical Ctr. Buffalo, New York, United States, 14260 Beth Israel Med. Ctr. (Mt. Sinai) New York, New York, United States Univ. of Rochester ACTG CRS Rochester, New York, United States United States, North Carolina Unc Aids Crs Chapel Hill, North Carolina, United States, 27514 Wake County Health and Human Services CRS Raleigh, North Carolina, United States United States, Ohio Univ. of Cincinnati CRS Cincinnati, Ohio, United States United States, Pennsylvania Hosp. of the Univ. of Pennsylvania CRS Philadelphia, Pennsylvania, United States United States, Washington University of Washington AIDS CRS Seattle, Washington, United States, 98104 Less <<
NCT02675465 Pompe Disease Phase 1 Phase 2 Recruiting September 2019 United States, Arizona ... More >> Neuromuscular Research Centre Recruiting Phoenix, Arizona, United States, 85028 Contact: Kumaraswamy Sivakumar    480-314-1007 ext 6    ksiva@nrcaz.com    Contact: Kristy Osgood    480-314-1007 ext 6    kosgood@nrcaz.com    Principal Investigator: Kumaraswamy Sivakumar          United States, California University of California Irvine Recruiting Orange, California, United States, 92868 Contact: Tahseen Mozaffar    714-456-2332    Mozaffar@uci.edu    Contact: Marie Wencel    714-456-2525    mwencel@uci.edu    Principal Investigator: Tahseen Mozaffar          United States, Florida University of Florida Recruiting Gainesville, Florida, United States, 32610 Contact: Barry J Byrne    352-273-6563    bbyrne@ufl.edu    Contact: Lee Kugelmann    352-273-6588    ekugelm@ufl.edu    Principal Investigator: Barry Byrne          United States, Georgia Emory University Division of Medical Genetics Completed Decatur, Georgia, United States, 30033 United States, Michigan Infusion Associates Recruiting Grand Rapids, Michigan, United States, 49525 Contact: Khan Nedd, MD    616-954-0600    khan.nedd@infusionassociates.com    Contact: Katie May    616-818-4473    katie.may@infusionassociates.com    Principal Investigator: Khan Nedd          United States, Montana Great Falls Clinic, LLP Recruiting Great Falls, Montana, United States, 59405 Contact: Karl Guter    406-771-3311    karl.guter@gfclinic.com    Contact: Jacob Decker    406-771-3373    jacob.decker@gfclinic.com    Principal Investigator: Karl Guter          United States, New Jersey Rutgers New Jersey Medical School Recruiting Newark, New Jersey, United States, 08103 Contact: Xue Ming    973-972-2922    mingxu@njms.rutgers.edu    Contact: Eliana Obando-Jaramillo    973-972-5435    emo65@njms.rutgers.edu    Principal Investigator: Xue Ming          United States, North Carolina Duke University Medical Center Recruiting Durham, North Carolina, United States, 27710 Contact: Priya Kishnani    919-684-2036    priya.kishnani@dm.duke.edu    Contact: Ela Stefanescu    919-681-4026    mihaela.stefanescu@duke.edu    Principal Investigator: Priya Kishnani          United States, Pennsylvania University of Pittsburgh Recruiting Pittsburgh, Pennsylvania, United States, 15213 Contact: Paula Clemens    412-648-9762    clempr@upmc.edu    Contact: Gabriela A Niizawa    412-383-9775    niizawaga@upmc.edu    Principal Investigator: Paula Clemens          United States, Virginia Lysosomal & Rare Disorders Research & Treatment Center (LDRTC) Recruiting Fairfax, Virginia, United States, 22030 Contact: Ozlem Goker-Alpan, MD    571-308-1925    ogoker-alpan@ldrtc.org    Contact: Jacqueline Fikry    703-261-6220 ext 105    jfikry@ldrtc.org    Principal Investigator: Ozlem Goker-Alpan          Australia, South Australia Womens & Childrens Hospital, Adelaide Active, not recruiting North Adelaide, South Australia, Australia, 05006 Germany University Children's Hospital Department of Neuropediatrics and Inborn Metabolic Disorders, St. Josefs-Hospital Recruiting Bochum, Germany, 44791 Contact: Peter Schwenkreis    +49 (0) 176 55 12 95 38    peter.schwenkreis@bergmannsheil.de    Contact: Rebecca Trost    +49 234 3023139    rebecca.trost@bergmannsheil.de    Principal Investigator: Schwenkreis Peter          Friedrich-Baur-Institure, Dep of Neurology - University Munich Recruiting Munich, Germany, 80336 Contact: Benedikt Schoser    +49 (0) 89 4400 57400    benedikt.schoser@med.uni-muenchen.de    Contact: Stephan Wenninger    +49 (0) 89 4400 57470    Stephan.Wenninger@med.uni-muenchen.de    Principal Investigator: Benedikt Schoser          Netherlands Erasmus Medical Center Recruiting Rotterdam, Netherlands Contact: A.T. van der Ploeg    31107037254    a.vanderploeg@erasmusmc.nl    Contact: Jacqueline Hardon    31107037047    j.hardon@erasmusmc.nl    Principal Investigator: A.T. van der Ploeg          United Kingdom University Hospital Birmingham NHS Foundation Trust, Queen Elizabeth Medical Center Completed Birmingham, United Kingdom, B15 2TH Salford Royal NHS Foundation Trust Recruiting Salford, United Kingdom, M6 8HD Contact: Mark Roberts    0161-206-4365    mark.roberts@srft.nhs.uk    Contact: Catherine Wilson    44- 01612064851    Catherine.Wilson@srft.nhs.uk    Principal Investigator: Mark Roberts Less <<
NCT03729362 Pompe Disease (Late-onset) Phase 3 Recruiting January 2021 United States, Arizona ... More >> Neuromuscular Research Center Not yet recruiting Phoenix, Arizona, United States, 85028 United States, California University of California, Irvine Recruiting Irvine, California, United States, 92868 United States, Virginia Lysosomal and Rare Disorders Research Recruiting Fairfax, Virginia, United States, 22030 Less <<
NCT00316498 Niemann Pick Diseases Phase 1 Completed - United States, Maryland ... More >> National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States, 20892 United States, New York Columbia University New York, New York, United States, 10032-3784 United Kingdom Oxford GlycoSciences Ltd. Abingdon, United Kingdom Less <<
NCT00001993 HIV Infections Phase 2 Completed - United States, Florida ... More >> Univ of Miami School of Medicine Miami, Florida, United States, 331361013 United States, Illinois Rush Presbyterian - Saint Luke's Med Ctr Chicago, Illinois, United States, 60612 United States, Indiana Infectious Diseases Research Clinic / Indiana Univ Hosp Indianapolis, Indiana, United States, 46202 United States, Ohio Ohio State Univ Hosp Clinic Columbus, Ohio, United States, 432101228 United States, South Carolina Julio Arroyo West Columbia, South Carolina, United States, 29169 United States, Washington Univ of Washington Seattle, Washington, United States, 981224304 Less <<
NCT00000692 HIV Infections Phase 1 Completed - United States, California ... More >> Univ of California / San Diego Treatment Ctr San Diego, California, United States, 921036325 Stanford Univ School of Medicine Stanford, California, United States, 94305 United States, Florida Univ of Miami School of Medicine Miami, Florida, United States, 331361013 United States, Illinois Rush Presbyterian - Saint Luke's Med Ctr Chicago, Illinois, United States, 60612 United States, Massachusetts Harvard (Massachusetts Gen Hosp) Boston, Massachusetts, United States, 02114 United States, South Carolina Julio Arroyo West Columbia, South Carolina, United States, 29169 Less <<
NCT00041535 Gaucher Disease PHASE2 COMPLETED 2007-03-21 National Institutes of Health ... More >>Clinical Center, 9000 Rockville Pike, Bethesda, Maryland, 20892, United States|Institute of Child Health, London, United Kingdom Less <<
NCT00194649 Contraception Phase 4 Completed - United States, Washington ... More >> University of Washington Seattle, Washington, United States, 98195 Less <<
NCT01451879 - Completed - United States, Florida ... More >> University of Florida Gainesville, Florida, United States, 32610 Less <<
NCT00002079 HIV Infections Phase 2 Completed - United States, California ... More >> Dr Marcus Conant San Francisco, California, United States, 94115 Shared Med Research Foundation Tarzana, California, United States, 91356 United States, Florida Stratogen of South Florida Miami Beach, Florida, United States, 33140 Saint Joseph's Hosp / Infectious Disease Rsch Institute Tampa, Florida, United States, 33614 United States, Georgia West Paces Clinical Research Incoporated Atlanta, Georgia, United States, 30327 United States, Pennsylvania Dr Samuel W Golden Pittsburgh, Pennsylvania, United States, 15218 United States, Texas Dallas Veterans Administration Med Ctr Dallas, Texas, United States, 75216 Dr Daniel Barbero Fort Worth, Texas, United States, 76104 Park Plaza Hosp Houston, Texas, United States, 77004 Less <<
NCT00537602 Cystic Fibrosis Phase 2 Terminated(Methodology applied... More >> did not meet all criteria required per guidelines) Less << - Spain ... More >> Corporacio Parc Tauli / Parc Tauli Hospital Barcelona, Spain Less <<
NCT00672022 GM2 Gangliosidoses ... More >> Tay-Sachs Sandhoff Disease Less << Phase 3 Completed - United States, District of Col... More >>umbia Children's National Medical Center Washington, District of Columbia, United States, 20010 Less <<
NCT00945347 Cystic Fibrosis Phase 2 Completed - Belgium ... More >> Cliniques Universitaires St Luc (Université Catholique de Louvain) 10 avenue Hippocrate Brussels, Belgium, 1200 Less <<
NCT01822028 Diarrhea Phase 1 Completed - Canada, Ontario ... More >> BioPharma Services Inc. Toronto, Ontario, Canada, M9L 3A2 Less <<
NCT02030015 GM1 Gangliosidoses ... More >> GM2 Gangliosidoses Tay-Sachs Disease Sandhoff Disease Less << Phase 4 Recruiting August 31, 2019 United States, Minnesota ... More >> University of Minnesota Recruiting Minneapolis, Minnesota, United States, 55455 Contact: Jeanine R. Jarnes, PharmD    612-626-5131    utzx0002@umn.edu    Principal Investigator: Jeanine R. Jarnes, PharmD          Sub-Investigator: Chester B. Whitley, MD, PhD Less <<
NCT00418847 Gangliosidoses GM2 Phase 2 Completed - Canada, Ontario ... More >> The Hospital for Sick Children Toronto, Ontario, Canada, M5G 1X8 Less <<
NCT00319046 Gaucher Disease Type 1 Phase 3 Completed - -
NCT00319046 - Completed - -
NCT00742092 Cystic Fibrosis Phase 2 Completed - Belgium ... More >> Universite Catholique de Louvain Brussels, Belgium, B-1200 Less <<
NCT02185651 Pompe Disease ... More >> Hypersensitivity Reaction Less << Phase 1 Terminated(Participants not in... More >>terested in enrolling.) Less << - -
NCT00517153 Niemann-Pick Type C Disease Phase 2 Completed - United States, New York ... More >> Columbia University Medical Center New York, New York, United States, 10032 Less <<
NCT01760564 Niemann-Pick Disease Type C Phase 3 Completed - Taiwan ... More >> National Taiwan University Hospital Taipei, Taiwan Less <<
NCT02520934 Gaucher Disease Not Applicable Active, not recruiting December 2018 Taiwan ... More >> National Taiwan University Hospital Taipei, Taiwan, 10041 Less <<
NCT02325362 Cystic Fibrosis Phase 2 Phase 3 Completed - France ... More >> Assistance publique-Hôpitaux de Paris, Hôpital Cochin Paris, France, 75014 Less <<

Protocol

Bio Calculators
Preparing Stock Solutions 1mg 5mg 10mg

1 mM

5 mM

10 mM

4.56mL

0.91mL

0.46mL

22.80mL

4.56mL

2.28mL

45.60mL

9.12mL

4.56mL

References

 

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